Rare Diseases

FDA Authorizes Emergency Use of Remdesivir to Treat COVID-19

by Samantha McGrail

FDA recently granted emergency use authorization (EUA) to Gilead for the investigational antiviral, remdesivir, to treat COVID-19 patients.  For more coronavirus updates, visit our resource...

FDA Approves Selumetinib for Rare Pediatric Neurofibromatosis

by Samantha McGrail

FDA recently approved the first treatment for pediatric patients with neurofibromatosis phase 1 (NF1), a rare disease that affects children.  NF1 is a rare, progressive condition of the nervous...

Sanofi, GSK Partner to Develop Adjuvanted COVID-19 Vaccine

by Samantha McGrail

Sanofi and GSK recently announced that they signed a letter of intent to develop an adjuvanted COVID-19 vaccine.  For more coronavirus updates, visit our resource page, updated twice daily...

Manufacturing Costs of Potential COVID-19 Drugs as Low as $1

by Samantha McGrail

Repurposed generics show promise as potential COVID-19 drugs and may be manufactured profitably at very low costs, according to a recent study.  For more coronavirus updates, visit...

Early Data Indicates Remdesivir is a Promising COVID-19 Drug

by Samantha McGrail

A recent study found that 68 percent of COVID-19 patients who received compassionate-use remdesivir showed clinical improvement, but measurements of efficacy will require ongoing controlled trials to...

NIH Launches Clinical Trial of Hydroxychloroquine for COVID-19

by Samantha McGrail

A clinical trial to evaluate the safety and efficacy of hydroxychloroquine for the treatment of hospitalized adult COVID-19 patients has begun, according to a recent press release from the National...

Pfizer Commits $40M in Grants to Combat COVID-19 Pandemic

by Samantha McGrail

The Pfizer Foundation recently announced the commitment of $40 million in medical and charitable cash grants to help combat the global health effects of the COVID-19 pandemic.  For more...

Henry Ford to Study Use of Hydroxychloroquine to Prevent COVID-19

by Samantha McGrail

Henry Ford Health System will lead the first large-scale study in the US to determine the effectiveness of hydroxychloroquine in preventing COVID-19 among healthcare workers and first...

4 of the Most Promising COVID-19 Vaccines In Development

by Samantha McGrail

The US currently has the most coronavirus cases of any country, with more than 330,000 individuals diagnosed with the virus, according to the CDC . Those are just the known cases, but experts...

Key Prescription Drugs Being Used to Treat COVID-19 Patients

by Samantha McGrail

As the number of confirmed COVID-19 cases continues to grow, pharmaceutical companies are boosting their efforts to combat the virus. There are currently over 245,000 cases of coronavirus in the US, a...

Graphics Processing Units Tech to Accelerate COVID-19 Sequencing

by Samantha McGrail

Genome-sequencing software NVIDIA announced that it will provide a free 90-day license to Parabricks to any researcher worldwide for rapid  COVID-19 sequencing, according to a recent press...

Lopinavir- Ritonavir Not Effective in Adults with Severe COVID-19

by Samantha McGrail

Hospitalized adult patients with confirmed COVID-19, experienced no benefits in lopinavir- ritonavir treatment compared to standard care, according to a recent clinical trial, LOTUS China...

$125M Initiative to Boost Drug Discovery for COVID-19 Treatment

by Samantha McGrail

The Bill and Melinda Gates Foundation, Wellcome, and Mastercard recently launched an initiative to boost drug discovery and biologics to treat patients with COVID-19. For more coronavirus updates,...

FDA, FTC Warn Companies to Stop Selling Fraudulent COVID-19 Drugs

by Samantha McGrail

The US Food and Drug Administration (FDA) and the Federal Trade Commission (FTC) issued warning letters to seven companies for selling false coronavirus (COVID-19) drugs, vaccines, and other products,...

FDA Provides Coronavirus Supply Chain Update

by Samantha McGrail

As the FDA closely monitors the coronavirus supply chain, it has uncovered a drug shortage related to a site affected by the coronavirus, or COVID-19, according to a recent statement from Stephen M....

Former SARS, MERS Drug Could Treat COVID-19 Patients

by Samantha McGrail

Remdesivir is effective in treating Middle East respiratory syndrome (MERS) and severe acute respiratory syndrome (SARS), but also may be a successful drug for patients with coronavirus, or COVID-19,...

HHS, J&J Partner to Boost Vaccination Discovery for Coronavirus

by Samantha McGrail

Janssen Pharmaceutical Companies will expand its partnership with Department of Health and Human Services (HHS) to accelerate a vaccination discovery for the coronavirus or COVID-19, Johnson &...

FDA Aims to Bolster Gene Therapy Development with New Guidance

by Ana Mulero

US Food and Drug Administration (FDA) recently issued six final guidances and draft guidance to advance gene therapy development by clarifying the policy framework for development and...

Top 5 Life Sciences Companies by Pharmaceutical Sales

by Kyle Murphy, PhD

The pharmaceutical industry is inching closer to the $1.3 trillion mark, with future growth anticipated for life sciences companies worldwide. According to the IQVIA Institute, the global...

Guidelines Call for Patient-Reported Outcomes in Clinical Trials

by Sara Heath

Clinical trial research outcomes need to be more patient-centered and integrate more patient-reported outcomes, according to a new set of research principles designed by the American College of...